How DMD Hub works with the pharmaceutical industry in delivering DMD research trials in the UK

DMD Hub aims to expand clinical research for Duchenne muscular dystrophy (DMD) in the UK – and works with the pharmaceutical industry in achieving this aim.

Why we work together 

DMD is a devastating condition which there is currently no cure or effective treatment for. The best hope for someone with DMD is access to a trial of a new treatment or therapy. 

Expanding clinical research for DMD in the UK will give more people with it opportunities to access trials. 

Crucially, it will also support research for better treatments. 

The pharmaceutical industry is a key part of enabling that, and we want to do all we can to support its DMD research in the UK. 

How we support pharmaceutical research trials 

We work collaboratively with pharmaceutical companies to give them the advice and support they need to make it easy as possible to successfully set up and run DMD clinical trials. 

We can offer pharmaceutical companies looking to run DMD trials in the UK help in four key areas:

Advice and support with trial administration

Development of site infrastructure 

  • We can provide advice and support on setting up trials to ensure that the requirements for DMD clinical trials set by industry are met.
  • We can assist with navigating the approvals process.
  • We can review trial application documentation. 
  • We can help with developing trial protocols. 
  • We can support in identifying trial sites.
  • We can support trial site capacity assessments. 
  • We can offer trial sites. 
  • We can develop and fund new trial sites. 

Ensuring staff readiness 

Recruitment of and liaison with patients 

  • We can provide training and mentoring to staff. 
  • We can fund staff to carry out trials. 
  • We can help you promote your trial opportunities to the DMD patients.
  • We can help with recruitment, matching eligible patients to your trials at DMD Hub sites. 
  • We can support your communications to the DMD community, including updates on the progress of trials and research outcomes. 


How we can work with your company 

We have the shared aim with companies undertaking DMD research – successful trials for new and effective DMD treatments and therapies. 

We have successfully worked with a wide range of companies on delivering DMD trials in the UK, including Pfizer, Roche, Santhera, Italfarmaco, Dyne Therapeutics, Vertex Pharmaceuticals and Solid Biosciences.

If you are looking to run DMD trials in the UK, we invite you to work with us. 

We can tailor our support to the needs of your company and trials. We are solution focused and can develop innovative new ways of delivering trials. 

If you would like to know more about DMD Hub and how we can work with you, contact Emma Heslop, DMD Hub Manager 


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